Learning through shared experience: Gene therapy for Haemophilia B

ISTH, 32nd Annual Congress, June 22–26, 2024

Watch the full recording of the “Gene Therapy for Haemophilia B” Product Theatre, held by CSL Behring at ISTH in June 2024 in Bangkok, Thailand, for an up-to-date overview of the current gene therapy landscape for haemophilia B.

Steven Pipe begins the session with an overview of the gene therapy products currently approved for haemophilia B and a summary of the clinical trial data and patient outcomes. Doris Quon then presents an overview of the patient and physician gene therapy journey and the ways in which it is expected that real-world experiences will differ to clinical trials.

In the second half of the session, Steven Pipe, Doris Quon and Daan Breederveld share their personal experiences of gene therapy for haemophilia B in a discussion that covers the patient journey from decision-making and setting expectations, the experience on the day of infusion from both patient and physician perspectives, through to the post-infusion monitoring and life changes experienced by patients following gene therapy.